A phase I-II trial of Cryopreserved Autologous CD34+ Haematopoietic Stem Cells Transduced ex vivo with a Lentiviral Vector Encoding for Human IDS.ApoEII in patients with neuronopathic Mucopolysaccharidosis Type II

Project Details

StatusActive
Effective start/end date1/05/2430/04/28

Funding

  • University of Manchester: £190,625.00