Mutant induced pluripotent stem cell lines recapitulate aspects of TDP-43 proteinopathies and reveal cell-specific vulnerability

Bilada Bilican, Andrea Serio, Sami J Barmada, Agnes Lumi Nishimura, Gareth J Sullivan, Monica Carrasco, Hemali P Phatnani, Clare A Puddifoot, David Story, Judy Fletcher, In-Hyun Park, Brad A Friedman, George Q Daley, David J A Wyllie, Giles E Hardingham, Ian Wilmut, Steven Finkbeiner, Tom Maniatis, Christopher E Shaw, Siddharthan Chandran

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